Hemgenix (etranacogene dezaparvovec-drlb) - CSL Behring
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Adstiladrin (nadofaragene firadenovec-vncg) - Ferring
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Zolgensma (onasemnogene abeparvovec-xioi) - Novartis
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Kebilidi (eladocagene exuparvovec-tneq) - PTC Therapeutics
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Roctavian (valoctocogene roxaparvovec-rvox) - BioMarin
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Elevidys (delandistrogene moxeparvovec-rokl) - Sarepta Therapeutics, Roche
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Glybera (alipogene tiparvovec) - uniQure, Chiesi, Xenon
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Luxturna (voretigene neparvovec-rzyl) - Novartis, Roche
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