Juxtapid (lomitapide) - Novelion, Chiesi
Evkeeza (evinacumab-dgnb) - Regeneron
LDL-C target achievement after adding evinacumab in 2 patients with autosomal recessive hypercholesterolemia. (PubMed, J Clin Lipidol) - Mar 4, 2026 - "These cases demonstrate a marked and clinically meaningful LDL-C-lowering effect of evinacumab in ARH, supporting its use as an effective LDL-R-independent therapeutic option." 
Journal • Atherosclerosis • Cardiovascular • Dyslipidemia • Familial Hypercholesterolemia • Genetic Disorders • Homozygous Familial Hypercholesterolemia • Metabolic Disorders
http://www.ncbi.nlm.nih.gov/pubmed/41775618
 
Antonia Albertí; Cesare Riccardo Sirtori; Chiara Moschetti; Chiara Pavanello; Francesco Vicari; Giuliana Germana Mombelli; Laura Calabresi
 
Mar 4, 2026
 
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