Long-term safety and efficacy of pegunigalsidase alfa in treatment-naive Fabry disease patients in F60/BRILLIANCE trial

Elfabrio (pegunigalsidase alfa-iwxj) - Protalix, Chiesi

https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70230

Ozlem Goker-Alpan 1; John A Bernat 2; Robert J Hopkin 5; Derralynn Hughes 4; Aleš Linhart 5; Antonio Pisani 6; Camilla Tøndel 7; William R Willcox 8; Irene Koulinska 9; David Lee 10; Irene Rastelletti 11; Eric L Wallace 12

Aug 17, 2026