Brineura (cerliponase alfa) - BioMarin
https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70230
 
Angela Schulz 1,2; Emily de los Reyes 5; Paul Gissen 4; Nicola Specchio 5; Raymond Y Wang 6; Alice Lail 7; Viviane Wang 7; Sherif Khattab 7
 
Jul 28, 2026
 
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