A phase 3, randomized, double-blind, placebo-controlled, multicenter study to evaluate the efficacy and safety of vosoritide in children with hypochondroplasia: CANOPY HCH-3 study design.

Voxzogo (vosoritide) - BioMarin

http://www.ncbi.nlm.nih.gov/pubmed/42694461

Andrew Dauber; Ian Sabir; Mohamad Maghnie; Moira Cheung; Noriyuki Namba; Oliver Semler; Ravi Savarirayan; Ricki Carroll; Roberto Bassi; Sajda Ghani; Valérie Cormier-Daire

Sep 5, 2026