Efficacy and safety of pegvaliase in adolescents with phenylketonuria: interim results from PEGASUS part 2

Palynziq (pegvaliase-pqpz) - BioMarin

https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70230

Amarilis Sanchez-Valle 1; Ashley Andrews 2; Julia B Hennermann 5; Jasmine Knoll 4; Yuri A Zarate 5; Dammie Brown 6; Konstantia-Maria Chevele 7; Kristin Lindstrom 6; Naomi RM Schwartz 6; Janet A Thomas 8

Aug 17, 2026