Clinical stabilisation in two patients with infantile-onset Pompe disease treated with cipaglucosidase alfa and miglustat

Rituxan (rituximab) - Roche

Pombiliti (cipaglucosidase alfa-atga) - BioMarin

methotrexate - Generic mfg.

Myozyme (alglucosidase alfa) - Sanofi

Tamara Žigman 1,2; Danijela Petković Ramadža 1,2; Ivana Čulo Čagalj 5; Ivan Bambir 1; Ivana Orbanić 4; Ivo Barić 1,2

Aug 17, 2026