Palynziq (pegvaliase-pqpz) - BioMarin
https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70230
 
Hadley Morotti 1; Shawn E. Christ 2; Uta Lichter-Konecki 5; Darren M. Janzen 1; Matthew Kivel 1; Cary O. Harding 1; additional individual contributors of the PHEFREE Consortium
 
Aug 17, 2026
 
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