MTE #24: Gene Therapies and Hepatotoxicity (Ticketed)

Hemgenix (etranacogene dezaparvovec-drlb) - CSL Behring

Beqvez (fidanacogene elaparvovec-dzkt) - Pfizer

Zolgensma (onasemnogene abeparvovec-xioi) - Novartis

Roctavian (valoctocogene roxaparvovec-rvox) - BioMarin

Elevidys (delandistrogene moxeparvovec-rokl) - Sarepta Therapeutics, Roche

Casgevy (exagamglogene autotemcel) - Vertex, CRISPR Therap

Tamir Diamond; Rajender Reddy

Aug 4, 2026