Reblozyl (luspatercept-aamt) - BMS, Merck (MSD)
Zynteglo (betibeglogene autotemcel) - Genetix Biotherapeutics
Pyrukynd (mitapivat) - Agios Pharmaceuticals
Casgevy (exagamglogene autotemcel) - Vertex, CRISPR Therap
etavopivat (NN7535) - Novo Nordisk
http://www.ncbi.nlm.nih.gov/pubmed/42584024
 
Ali T Taher; Franco Locatelli; Khaled M Musallam; Maria Domenica Cappellini; Mattia Algeri
 
Aug 13, 2026
 
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