ASC618, a Second Generation of FVIII Gene Therapy for Hemophilia A, Exhibits Major Transduction and Transgene Expression in the Target Liver Tissues: Results of IND-Enabling Pharmacokinetics Studies in Mice and Non-Human Primates

ASC-618 - Applied StemCell, Expression Therap

Chengtao Yang; Tanvee Sawant; Avital Gilam; Yin Zhang; Eliza Dewangan; Milena Veselinovic; Ruhong Jiang; H. Steve Zhang; Zoya Gluzman-Poltorak

Apr 20, 2022