Intravenous Administration of FBX-101 (AAVrh10. hGALC) Following Hematopoietic Stem Cell Transplantation, a Potential Treatment for Infantile Krabbe Disease: RESKUE Phase 1/2 Clinical Trial

FB-101 - 1ST Bio, D&D Pharmatech

https://2022.myana.org/sites/default/files/images/2022/ana_v92_is29_rev2.pdf

Maria L. Escolar, MD1; Randy Windreich, Dr.2; Michelle Poe, Ph.D.2; Keith Werling, Ph.D.2; Erandi De Silva, Ph.D.1; Juan Ruiz, M.D.1; Paul Szabolcs, M.D.2

Oct 17, 2022