Tegsedi (inotersen) - Ionis, SOBI
Onpattro (patisiran) - Alnylam, Sanofi
Vyndaqel (tafamidis meglumine) - Pfizer
Amvuttra (vutrisiran) - Alnylam
http://www.ncbi.nlm.nih.gov/pubmed/40940654
 
Bettina Heidecker; Duc Chu Dieu; Gina Barzen; Harisa Muratovic; Helena F Pernice; Katrin Hahn; Nicolas W Wieder; Paul J Wetzel; Sebastian Spethmann; Stefanie M Werhahn
 
Sep 13, 2025
 
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