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Oxlumo (lumasiran) - Alnylam
Onpattro (patisiran) - Alnylam, Sanofi
https://www.aasld.org/the-liver-meeting/sessions/basic-science-workshop-ribonucleic-acid-nanomedicine-reprogramming-cells-to-transform-liver-outcomes-part-1-cutting-edge-tools-for-liver-gene-editing-559392
Mamatha Bhat, M.D.; Reben Raeman, MS, PhD
Aug 29, 2025
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