Onpattro (patisiran) - Alnylam, Sanofi
Vyndaqel (tafamidis meglumine) - Pfizer
Amvuttra (vutrisiran) - Alnylam
https://www.aan.com/msa/Public/Events/AbstractDetails/64138
 
Lamees Alhallaq1; J. David Avila2
 
Mar 6, 2026
 
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