Tegsedi (inotersen) - Ionis, SOBI
Attruby (acoramidis) - BridgeBio
Wainua (eplontersen) - Ionis, AstraZeneca
Onpattro (patisiran) - Alnylam, Sanofi
Vyndaqel (tafamidis meglumine) - Pfizer
Amvuttra (vutrisiran) - Alnylam
http://www.ncbi.nlm.nih.gov/pubmed/41149834
 
Darren M Nguyen; Gurpreet Sodhi; Noyan Ramazani; Tahir Tak
 
Oct 29, 2025
 
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