rebisufligene etisparvovec (UX111) - Ultragenyx
https://onlinelibrary.wiley.com/doi/epdf/10.1002/jimd.70230
 
Maria J. de Castro Lopez 1; Heather A. Lau 2; Kaushik Patra 2; Melissa Wolf 2; Nicholas J. C. Smith 5; Maria L. Couce 1; Deepa S. Rajan 4; Kristen V. Truxal 5; Kim L. McBride 5,6; Maria Fuller 7; Eines Monteagudo 8; Lucy Dougherty 9; Mireia del Toro 9; Kevin M. Flanigan 5
 
Jul 28, 2026
 
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