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rebisufligene etisparvovec (UX111) - Ultragenyx
https://pag.virtual-meeting.org/US/asgct2026/en-US/pag/presentation/685750
Shivakumar Pattada1; Tianhong Yang1; Jorge Ayala1; Rachel Hamptom1; Eddie Hamptom1; Mario Sanchez1; Kassandra Riley1; Walter Acosta1; Carole Cramer1
Apr 13, 2026
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