The reiMMAgine Study: Evaluation of the Safety, Tolerability, and Pharmacodynamics of AAV8 Gene Therapy (MMA-101) in Combination with an Immunotolerance-Inducing Nanoparticle (ImmTOR) in MUT Subtype Isolated Methylmalonic Acidemia (MMA)

eRapa (encapsulated rapamycin) - Emtora Biosci

sirolimus - Generic mfg.

Rehan Azeem1; Irini Manoli2; Alicia Michaud3; Jennifer L. Sloan4; Sheri Rhodes1; Sheldon Leung3; Charles P. Venditti2; Peter G. Traber1

Apr 21, 2023