Nurzigma (pridopidine) - Prilenia
AMT-130 - uniQure
SKY-0515 - Skyhawk Therap
votoplam (HTT227) - Novartis
RG6662 - Roche
tominersen (RG6042) - Roche
http://www.ncbi.nlm.nih.gov/pubmed/41295902
 
Edward J Wild; Mena Farag; Sarah J Tabrizi
 
Nov 26, 2025
 
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