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Hemgenix (etranacogene dezaparvovec-drlb) - CSL Behring
Beqvez (fidanacogene elaparvovec-dzkt) - Pfizer
dalnacogene ponparvovec (BBM-H901) - Belief Biomed
http://www.ncbi.nlm.nih.gov/pubmed/41381305
Bingjie Ding; Hongkai Jia; Hu Zhou; Xuewen Song
Dec 12, 2025
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