surabgene lomparvovec (ABBV-RGX-314) - REGENXBIO, AbbVie
JNJ-1887 - J&J
ixoberogene soroparvovec (ADVM-022) - Adverum Biotech
GT-005 - Pentixapharm
PPY988 - Novartis
http://www.ncbi.nlm.nih.gov/pubmed/40601510
 
Henry W Zhou; Leo A Kim
 
Jul 2, 2025
 
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