apazunersen (GTX-102) - Foundation for Angelman Syndrome Therap, Ultragenyx
dexamethasone - Generic mfg.
https://acmg.planion.com/Web.User/AbstractDet?ACCOUNT=ACMG&ABSID=888860&CONF=AM26&ssoOverride=OFF&CKEY=O4O0G3O53
 
Kimberly Goodspeed; Tricia Cimms, MPH; Angel Chen, MS; Wen-Hann Tan, BMBS; Kenneth A. Myers, MD, PhD, FRCPC, CSCN; Elizabeth M. Berry-kravis, MD, PhD; Deike Weiss, Dr. med.; Laurent Servais, MD, PhD; Erick Sell, MD
 
Jan 8, 2026
 
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