renizgamglogene autogedtemcel (EDIT-301) - Editas Medicine
https://library.ehaweb.org/eha/2025/eha2025-congress/4161194/anshul.gupta.targeted.lipid.nanoparticle.delivery.enables.in.vivo.hbg1.2.html?f=menu%3D6%2Abrowseby%3D8%2Asortby%3D2%2Amedia%3D3%2Ace_id%3D2882%2Aot_id%3D31575%2Amarker%3D5844%2Afeatured%3D19595
 
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