VQ-101 - Vanqua Bio
https://www.mdsabstracts.org/abstract/vq-101-a-cns-penetrant-small-molecule-allosteric-activator-of-glucocerebrosidase-gcase-demonstrates-favorable-tolerability-and-sustained-activation-of-lysosomal-gcase-in-individuals-with-parkinson/
 
M. Facheris; D. Ysselstein; J. van Dervalk; E. Thijssen; L. Pagan; G. Valstar; C. Schotborgh; P. Kremer; M. Hagey; J. Cederbaum; J. Sullivan; K. Hunt; O. Siddiqui
 
Oct 16, 2025
 
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