Casgevy (exagamglogene autotemcel) - Vertex, CRISPR Therap
CTx001 - Complement Therap
http://www.ncbi.nlm.nih.gov/pubmed/41377064
 
Athanasios Didangelos; Dennis Keefe; Ewa Szula; Mustafa M Munye; Nakul Patel; Pamela Whalley; Parisa Zamiri; Paul N Bishop; Peter Emery-Billcliff; Rachel Green; Rafiq Hasan; Richard D Unwin; Simon J Clark; Sofiya Pisarenka; Sonika Rathi; Stamatia Zafeiri; Viranga Tilakaratna
 
Dec 11, 2025
 
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