SGT-003 - Solid BioSci
fordadistrogene movaparvovec (PF-06939926) - Pfizer
GNT 0004 - Sarepta Therap
Elevidys (delandistrogene moxeparvovec-rokl) - Sarepta Therap, Roche
RGX-202 - REGENXBIO
http://www.ncbi.nlm.nih.gov/pubmed/41391912
 
V Laugel
 
Dec 15, 2025
 
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