hydroxyurea - Generic mfg.
sapablursen (IONIS-TMPRSS6-Lrx) - Ono Pharma
INCA033989 - Incyte
rusfertide (PTG-300) - Protagonist Therap, Takeda
Besremi (ropeginterferon alfa-2b-njft) - PharmaEssentia
JNJ-9968 - J&J
bomedemstat (MK-3543) - Merck (MSD)
Jakafi (ruxolitinib) - Incyte
Duvyzat (givinostat) - Italfarmaco
divesiran (SLN124) - Silence Therap
https://clml-25-01.elsevierdigitaledition.com/
 
Chi-Joan How, MD 1; Gabriela Hobbs, MD 2*
 
Aug 26, 2025
 
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