Nurzigma (pridopidine) - Prilenia
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DNL343 - Denali Therap
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fosigotifator (ABBV-CLS-7262) - AbbVie, Calico Life Sciences
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CNM-Au8 - Clene
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verdiperstat (BHV-3241) - Biohaven
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monepantel (NUZ-001) - Neurizon Therapeutics
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Zilbrysq (zilucoplan) - UCB
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Cabaletta (trehalose) - Seelos Therap
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