Tegsedi (inotersen) - Ionis, SOBI
Wainua (eplontersen) - Ionis, AstraZeneca
Oxlumo (lumasiran) - Alnylam
Viltepso (viltolarsen) - Nippon Shinyaku, National Center of Neurology and Psychiatry
Onpattro (patisiran) - Alnylam, Sanofi
Leqvio (inclisiran) - Novartis
Spinraza (nusinersen) - Biogen
Qfitlia (fitusiran) - Sanofi
Exondys 51 (eteplirsen) - Sarepta Therap
Givlaari (givosiran) - Alnylam
Qalsody (tofersen) - Biogen
Macugen (pegaptanib) - Bausch Health
Vyondys 53 (golodirsen) - Sarepta Therap
Izervay (avacincaptad pegol intravitreal solution) - Astellas
Dawnzera (donidalorsen sodium) - Ionis
Kynamro (mipomersen) - Kastle Therap
Tryngolza (olezarsen) - Ionis
Amvuttra (vutrisiran) - Alnylam
Amondys 45 (casimersen) - Sarepta Therap
Rivfloza (nedosiran) - Novo Nordisk
http://www.ncbi.nlm.nih.gov/pubmed/41394159
 
Ai-Ming Yu; Joseph M Cronin
 
Dec 15, 2025
 
Next