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Lyfgenia (lovotibeglogene autotemcel) - bluebird bio
Casgevy (exagamglogene autotemcel) - Vertex, CRISPR Therap, Molecular Templates
http://www.ncbi.nlm.nih.gov/pubmed/40757789
Abu-Baker Khalid Sharafeldin; Mohammed Kawari; Omer Tarig Fathi Abdelazim; Zahra Abdulla Isa Yusuf Hasan; Zainab Abdulmajeed Toorani
Aug 4, 2025
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