hydroxyurea - Generic mfg.
Oxbryta (voxelotor) - Pfizer
Lyfgenia (lovotibeglogene autotemcel) - bluebird bio
renizgamglogene autogedtemcel (EDIT-301) - Editas Medicine
Casgevy (exagamglogene autotemcel) - Vertex, CRISPR Therap, Molecular Templates
Adakveo (crizanlizumab-tmca) - Novartis
http://www.ncbi.nlm.nih.gov/pubmed/40146367
 
Fengjuan Xuan; Franco Locatelli; Haydar Frangoul; Michael J Eckrich; Nanxin Li; Stephan A Grupp; Suzan Imren
 
Mar 27, 2025
 
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