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BEAM-101 - Beam Therap
https://www.globenewswire.com/news-release/2025/06/03/3092605/0/en/Beam-Therapeutics-Announces-U-S-FDA-Orphan-Drug-Designation-Granted-to-BEAM-101-for-the-Treatment-of-Sickle-Cell-Disease.html
Jun 3, 2025
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