Niktimvo (axatilimab-csfr) - Syndax Pharma, Incyte
BEAM-101 - Beam Therap
Casgevy (exagamglogene autotemcel) - Vertex, CRISPR Therap
https://www.scri.com/news/sarah-cannon-research-institute-to-present-research-on-advances-in-blood-cancers-and-blood-disorders-at-2025-ash-annual-meeting--exposition/
 
Dec 2, 2025
 
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