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vanzacaftor (VX-121) - Vertex
Attruby (acoramidis) - BridgeBio
Vafseo (vadadustat) - Akebia Therap
Xolremdi (mavorixafor) - X4 Pharma, Norgine
Rezdiffra (resmetirom) - Madrigal Pharma
Lazcluze (lazertinib) - J&J
Ojemda (tovorafenib) - Day One Biopharma
Duvyzat (givinostat) - Italfarmaco
Iqirvo (elafibranor) - Ipsen
sulopenem etzadroxil/probenecid (CP-70429) - Iterum
Voydeya (danicopan) - AstraZeneca
Voranigo (vorasidenib) - Servier
Livdelzi (seladelpar) - Gilead
Exblifep (cefepime/enmetazobactam) - Allecra
http://www.ncbi.nlm.nih.gov/pubmed/41567854
Isabelle Ragueneau-Majlessi; Jingjing Yu; Katie Owens; Sophie Argon; Yan Wang
Jan 22, 2026
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