Zolgensma (onasemnogene abeparvovec-xioi) - Novartis
resamirigene bilparvovec (AT132) - Astellas
fordadistrogene movaparvovec (PF-06939926) - Pfizer
SGT-001 - Solid BioSci
LYS-SAF302 - Lysogene, Sarepta Therap
https://www.mdaconference.org/abstract-library/longitudinal-changes-of-anti-aav9-and-anti-aavrh74-antibodies-in-treated-and-untreated-patients/
 
Stephanie Salabarria; BHSc; University of Florida; Kirsten Coleman; MBA; University of Florida; Megan Wichman; BSc; University of Florida; Julie Berthy; DNP; University of Florida; Carmen Leon; MD; U of Florida; Manuela Corti; PT; PhD; University of Florida; Barry Byrne; MD; PhD; University of Florida
 
Feb 16, 2024
 
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