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Raynier Devillier, MD, PhD1; Regis Peffault De Latour2; Patrice Chevallier, MD3; Anne Huynh, MD4; Patrizia Chiusolo5; Aurelie Bauquet6; Laura Simons, MD, PhD7; Pierre Heimendinger8; Olivier Negre, PhD9; Shabi Soheili, PhD10; Juliette Paillet8; Isabelle Andre, PhD11; Sebastien Oster8; Marina Cavazzana, MD, PhD12,13; Frédéric François Lehmann8; Fabio Ciceri14
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