Vpriv (velaglucerase alfa) - Takeda
Vimizim (elosulfase alfa) - BioMarin
Evrysdi (risdiplam) - SMA Foundation, PTC Therap, Roche
Aldurazyme (laronidase) - BioMarin, Sanofi
Naglazyme (galsulfase) - AnGes MG, BioMarin
Myozyme (alglucosidase alfa) - Sanofi
https://www.ispor.org/heor-resources/presentations-database/presentation/intl2023-3666/125167
 
Piniazhko O1; Khmelovska M1; Serediuk V1; Malyshevska I1; Romanenko I1; Ioltukhovskyi I1; Masheiko A1; Babenko M1; Lobas M1; Kosyachenko K2; Kahveci R3
 
Mar 9, 2023
 
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