Elexacaftor/tezacaftor/ivacaftor improves CFTR function to near-normal levels in children with cystic fibrosis. (PubMed, Eur Respir J) - Sep 25, 2026 - "Our results show that treatment with ETI results in near-normal CFTR function measured in freshly obtained rectal biopsies in children with CF aged 2 to 11 years and at least one F508del allele."
Clinical • Journal • Cystic Fibrosis • Genetic Disorders • Immunology • Infectious Disease • Inflammation • Pulmonary Disease • Respiratory Diseases
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Alicia González; Jasmin Berger; Julian Berges; Marcus A Mall; Mirjam Stahl; Olaf Sommerburg; Rory E Morty; Simon Y Graeber; Stephanie Thee; Susanne Hämmerling; Virginia Rossow; Yin Yu
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