Trikafta (elexacaftor/tezacaftor/ivacaftor) - Vertex
Exocrine pancreatic function and highly effective modulators: A dual center retrospective study. (PubMed, J Pediatr Gastroenterol Nutr) - Sep 11, 2026 - "Clinically meaningful FE-1 improvement in established EPI appears limited, although a subset of younger patients may show meaningful improvement. HEMTs may also reduce pancreatitis recurrence in pancreatic-sufficient individuals." 
Journal • Retrospective data • Cystic Fibrosis • Genetic Disorders • Immunology • Pancreatitis • Pediatrics • Pulmonary Disease • Respiratory Diseases • CFTR
http://www.ncbi.nlm.nih.gov/pubmed/42720211
 
Alice Castaldo; Angela Sepe; Antonella Tosco; Chiara Cimbalo; Cristina Fevola; Daniela Dolce; Francesca Capasso; Gabriele Simonetti; Laura Salvadori; Raffaele Cerchione; Vito Terlizzi
 
Sep 11, 2026
 
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