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Zolgensma (onasemnogene abeparvovec-xioi) - Novartis
Evrysdi (risdiplam) - Roche
Spinraza (nusinersen) - Biogen
http://www.ncbi.nlm.nih.gov/pubmed/42759416
Christian A Surí-Báez; Emma C Laureta; Janice Lester; Kristin Kelly-Pieper; Madeleine Grigg-Damberger; Ruri Kitada; Sanjeev V Kothare
Sep 19, 2026
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