Evrysdi (risdiplam) - Roche
Spinraza (nusinersen) - Biogen
http://www.ncbi.nlm.nih.gov/pubmed/42727545
 
; Aleks Carver; Andi Thornton; Andria Merrison; Anne-Marie Childs; Annemarie Rohwer; Channa Hewamadduma; Chiara Marini-Bettolo; Clare M Galtrey; Dionne Moat; Elena Karkkainen; Francesco Muntoni; Gennadiy Ilyashenko; Giovanni Baranello; Grecia Benesperi; James B Lilleker; Jess Page; John McConville; Kate Adcock; Laura Simms; Lindsay Murphy; Liz Ryburn; Maria Elena Farrugia; Mariacristina Scoto; Matthew Parton; Portia Thorman; Robert Muni-Lofra; Stephanie Tanner
 
Sep 12, 2026
 
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