Serum circulating cell-free messenger RNA profile response to risdiplam treatment in adult patients with late-onset spinal muscular atrophy.

Evrysdi (risdiplam) - Roche

Spinraza (nusinersen) - Biogen

http://www.ncbi.nlm.nih.gov/pubmed/42798856

Andreas Roos; Christoph Kleinschnitz; Kai Christine Liebig; Linda-Isabell Schmitt; Markus Leo; Stefanie Hezel; Svenja Neuhoff; Tim Hagenacker; Tobias Ruck

Sep 27, 2026