Evrysdi (risdiplam) - Roche
Spinraza (nusinersen) - Biogen
Consensus for the Diagnosis and Treatment of Patients With Spinal Muscular Atrophy (SMA) in Latin America. (PubMed, Rev Neurol) - Oct 1, 2026 - "This consensus provides a practical and adaptable framework to optimize SMA care in LATAM, supporting longitudinal, patient-centered clinical decision-making." 
Journal • CNS Disorders • Gene Therapies • Genetic Disorders • Movement Disorders • Muscular Atrophy • Rare Diseases • SMA4 • SMN1 • SMN2
http://www.ncbi.nlm.nih.gov/pubmed/42812016
 
Alfonso P Gutiérrez Mata; Andrés E Nascimento Osorio; Carlos A Franco Toñanez; Carol J Zuniga García; Claudia Castiglioni; Conrado Medici; Diana Ramírez-Montaño; Edmar Zanoteli; Edna J Bobadilla Quesada; Edwin S Vargas Cañas; Eva S Pérez Almengor; Francisco Espinel; Graciela Barros Acevedo; Guilca Contreras Caicedo; Henry H Galvez Quiñonez; Javier E Linzoain; Jesús A Armijo Gómez; Jorge A Bevilacqua; Juliana Gurgel-Giannetti; Leticia M Munive Baez; Lourdes I Núñez Antelo; Marco J Casartelli Galeano; María C Hervias Ruz; María de Los Ángeles Beytía; María E Meza Cano; María Fernanda Cordero Molina; María R Gueçaimburu; Mariela A Lucero; Mario Gutiérrez-Saenz; Matilde Ruiz García; Nicholas Earle; Peggy C Martínez Esteban; Rodrigo Moreno-Salgado; Rogelio R Odales Ibarra; Rosa E Escobar Cedillo; Sandra C Mesa Restrepo; Sandra M Castellar-Leones; Soledad Monges; Verónica D Artiga-Rodríguez; Verónica Sáez Galaz
 
Oct 1, 2026
 
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