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Zolgensma (onasemnogene abeparvovec-xioi) - Novartis
Evrysdi (risdiplam) - Roche
Spinraza (nusinersen) - Biogen
http://www.ncbi.nlm.nih.gov/pubmed/42799810
Dongni Ye; Esteban Lemus Wirtz; John Meehan; Min Yang; Sandra Reyna; Walter Toro Jimenez; Wei Song
Sep 27, 2026
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