Qalsody (tofersen) - Biogen
Neurovascular Modulation of the Blood-brain Barrier Using Focused Ultrasound for Antisense Therapy Delivery in Amyotrophic Lateral Sclerosis. (PubMed, Curr Neurovasc Res) - Oct 14, 2026 - "MRI-guided FUS combined with CaP lipid nanoparticles represents a promising non-invasive platform for SOD1-targeted ASO delivery and precision gene therapy in ALS." 
Journal • Amyotrophic Lateral Sclerosis • CNS Disorders • Gene Therapies • Inflammation
http://www.ncbi.nlm.nih.gov/pubmed/42865191
 
Deepak Venkatraman; J Jaisudha; M K Vijayalakshmi; Sambasivam Gopinath; Sujit Kumar Mohanty; Tozer Meena Sandela; Vasanth Kumar Mohan
 
Oct 14, 2026
 
Prev Next