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Zolgensma (onasemnogene abeparvovec-xioi) - Novartis
Evrysdi (risdiplam) - Roche
Spinraza (nusinersen) - Biogen
http://www.ncbi.nlm.nih.gov/pubmed/42713019
Congyue Annie Peng; Emma W Crow; Madison M Sexton
Sep 10, 2026
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