Preclinical studies of an AAV8-CYP4V2 gene therapy VGR-R01 for the treatment of Bietti crystalline dystrophy.

VGR-R01 - Beijing Tongren Hospital

http://www.ncbi.nlm.nih.gov/pubmed/40927762

Liang Lu; Lu Guo; Nan Huang; Shin-Shay Tian; Wenjing Luo; Xi Zhu; Xiaoping Zhao; Yanrong Cao; Yezheng Tao; Yufei Zhang

Sep 10, 2025