Treating a patient with ADP porphyria through suppression of both hepatic and erythroid ALA production.

hydroxyurea - Generic mfg.

Givlaari (givosiran) - Alnylam

http://www.ncbi.nlm.nih.gov/pubmed/42443962

Edith C H Friesema; Eduard J van Beers; Janneke G Langendonk; Nicole C Peltenburg; Niels C Veldhoen

Jul 15, 2026