Long-term efficacy and safety of vutrisiran in hereditary transthyretin amyloidosis with polyneuropathy: final analysis of the HELIOS-A randomized treatment extension.

Amvuttra (vutrisiran) - Alnylam

http://www.ncbi.nlm.nih.gov/pubmed/42290201

Alejandra González-Duarte; Cécile Cauquil; Colleen Moffitt; David Adams; Julian Gillmore; Katherine Boyle; Laura Obici; Márcia Waddington-Cruz; Marianne Sweetser; Michelle Mezei; Prajakta Badri; Weizhi Zhao; Yoshiki Sekijima

Jun 16, 2026