Impact of enzyme replacement therapy and migalastat on disease progression in females with fabry disease.

Galafold (migalastat) - Amicus

Fabrazyme (agalsidase beta) - Sanofi

Replagal (agalsidase alfa) - Samaritan Pharma, Takeda

http://www.ncbi.nlm.nih.gov/pubmed/39980015

Albina Nowak; Anja Friederike Köhn; Christine Kurschat; Eva Brand; Jessica Kaufeld; Malte Lenders; Markus Cybulla; Nicole Maria Muschol

Feb 21, 2025