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Pombiliti (cipaglucosidase alfa-atga) - BioMarin
https://onlinelibrary.wiley.com/doi/10.1111/ene.70630
O. Musumeci 1; I. Arena 1; C. Sancricca 2; S. Servidei 2; A. Sechi 3; B. Risi 4; M. Filosto 4; L. Vercelli 5; T. Mongini 5; S. Fecarotta 6; G. Parenti 6; L. Ruggiero 7; G. Crescimanno 8; A. Toscano 1
Jun 12, 2026
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